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References from Strimvelis® for Treating Severe Combined Immunodeficiency Caused by Adenosine Deaminase Deficiency: An Evidence Review Group Perspective of a NICE Highly Specialised Technology Evaluation. Local targets link to admitted publications; unresolved targets remain external evidence.
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10.1182/blood-2011-12-396879
10.1182/blood-2011-12-396879 · 2012 · External reference
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2006 · External reference
10.1016/j.clim.2015.08.001
10.1016/j.clim.2015.08.001 · 2015 · External reference
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10.1007/s10875-017-0373-y
10.1007/s10875-017-0373-y · 2017 · External reference
10.1016/s0140-6736(09)60237-3
10.1016/s0140-6736(09)60237-3 · 2009 · External reference
10.1182/blood-2009-06-189209
10.1182/blood-2009-06-189209 · 2009 · External reference
10.1056/nejmoa1401177
10.1056/nejmoa1401177 · 2014 · External reference
10.1182/blood-2013-02-380105
10.1182/blood-2013-02-380105 · 2013 · External reference
10.1016/j.clim.2005.07.006
10.1016/j.clim.2005.07.006 · 2005 · External reference
10.1182/blood-2016-01-688226
10.1182/blood-2016-01-688226 · 2016 · External reference
10.1016/j.clim.2006.12.009
10.1016/j.clim.2006.12.009 · 2007 · External reference
10.1067/mpd.2001.115023
10.1067/mpd.2001.115023 · 2001 · External reference
10.1182/blood-2006-07-034678
10.1182/blood-2006-07-034678 · 2007 · External reference
10.1016/j.jpeds.2003.10.055
10.1016/j.jpeds.2003.10.055 · 2004 · External reference
10.1182/blood-2006-01-009241
10.1182/blood-2006-01-009241 · 2006 · External reference
10.1038/sj.bmt.1705054
10.1038/sj.bmt.1705054 · 2005 · External reference
10.1001/jama.295.5.508
10.1001/jama.295.5.508 · 2006 · External reference
10.1007/s10875-015-0191-z
10.1007/s10875-015-0191-z · 2015 · External reference
10.1016/j.jaci.2014.06.021
10.1016/j.jaci.2014.06.021 · 2014 · External reference
10.4049/jimmunol.1001770
10.4049/jimmunol.1001770 · 2010 · External reference
10.1016/j.jaci.2010.06.015
10.1016/j.jaci.2010.06.015 · 2010 · External reference
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10.1111/petr.12723
10.1111/petr.12723 · 2016 · External reference
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10.1126/science.1088547
10.1126/science.1088547 · 2003 · External reference
10.1172/jci35798
10.1172/jci35798 · 2008 · External reference
10.1038/sj.bmt.1703641
10.1038/sj.bmt.1703641 · 2002 · External reference
10.1111/ctr.12065
10.1111/ctr.12065 · 2013 · External reference
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