Research graph
References from CTGCT, Centre of Excellence for the Technologies of Gene and Cell Therapy: Collaborative translation of scientific discoveries into advanced treatments for neurological rare genetic diseases and cancer. Local targets link to admitted publications; unresolved targets remain external evidence.
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2022 · External reference
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10.1038/nbt1212-1153
10.1038/nbt1212-1153 · External reference
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10.1038/s41587-024-02166-7
10.1038/s41587-024-02166-7 · External reference
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10.3390/ijms232012564
10.3390/ijms232012564 · External reference
10.1016/j.ejmg.2024.104974
10.1016/j.ejmg.2024.104974 · External reference
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10.3390/cancers3033279
10.3390/cancers3033279 · External reference
10.1073/pnas.86.24.10024
10.1073/pnas.86.24.10024 · External reference
10.1016/j.retram.2017.08.003
10.1016/j.retram.2017.08.003 · External reference
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10.1080/2162402x.2020.1785608
10.1080/2162402x.2020.1785608 · External reference
10.3390/cancers13194785
10.3390/cancers13194785 · External reference
10.1016/j.omto.2020.04.009
10.1016/j.omto.2020.04.009 · External reference
10.1182/blood.2020009759
10.1182/blood.2020009759 · External reference
10.1136/jitc-2023-008155
10.1136/jitc-2023-008155 · External reference
10.1038/s41598-020-59082-4
10.1038/s41598-020-59082-4 · External reference
10.1016/j.jtct.2022.06.025
10.1016/j.jtct.2022.06.025 · External reference
10.1038/s41573-019-0038-z
10.1038/s41573-019-0038-z · External reference
10.1038/s41590-023-01665-0
10.1038/s41590-023-01665-0 · External reference
10.1016/j.omto.2023.04.005
10.1016/j.omto.2023.04.005 · External reference
10.1016/j.omton.2024.200815
10.1016/j.omton.2024.200815 · External reference
10.1038/s41421-023-00635-y
10.1038/s41421-023-00635-y · External reference
10.1038/s41589-022-01136-x
10.1038/s41589-022-01136-x · External reference
10.1126/science.1225829
10.1126/science.1225829 · External reference
10.1038/s41467-022-31386-1
10.1038/s41467-022-31386-1 · External reference
10.1038/s41434-023-00434-w
10.1038/s41434-023-00434-w · External reference
10.1038/s41586-019-1711-4
10.1038/s41586-019-1711-4 · External reference
10.1056/nejmoa2215643
10.1056/nejmoa2215643 · External reference
10.1038/s41551-022-00911-4
10.1038/s41551-022-00911-4 · External reference
10.1038/s41467-022-33157-4
10.1038/s41467-022-33157-4 · External reference
10.1038/s41586-021-03534-y
10.1038/s41586-021-03534-y · External reference
10.1016/j.jval.2022.12.014
10.1016/j.jval.2022.12.014 · External reference
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10.1212/wnl.0000000000011597
10.1212/wnl.0000000000011597 · External reference
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10.1038/s41571-022-00607-3
10.1038/s41571-022-00607-3 · External reference
10.1016/j.hlpt.2023.100752
10.1016/j.hlpt.2023.100752 · External reference
10.1038/s41467-022-32866-0
10.1038/s41467-022-32866-0 · External reference
10.1002/jgm.2747
10.1002/jgm.2747 · External reference