Research graph
References from Editing cells in place: Targeted in vivo gene editing of hematopoietic stem cells. Local targets link to admitted publications; unresolved targets remain external evidence.
Engineered lipid nanoparticles for in vivo and durable editing of haematopoietic stem cells within humanized mice
10.1038/s41551-026-01765-w · 2026 · External reference
Hematopoietic Stem Cell Gene Therapy: Progress and Lessons Learned
10.1016/j.stem.2017.10.010 · 2017 · External reference
A systematic review and meta-analysis of gene therapy with hematopoietic stem and progenitor cells for monogenic disorders
10.1038/s41467-022-28762-2 · 2022 · External reference
Hematopoiesis: a human perspective
10.1016/j.stem.2012.01.006 · 2012 · External reference
Genetic engineering meets hematopoietic stem cell biology for next-generation gene therapy
10.1016/j.stem.2023.04.014 · 2023 · External reference
Adaptation to ex vivo culture reduces human hematopoietic stem cell activity independently of the cell cycle
10.1182/blood.2023021426 · 2024 · External reference
Lipid nanoparticles for mRNA delivery
10.1038/s41578-021-00358-0 · 2021 · External reference
Bone-marrow-homing lipid nanoparticles for genome editing in diseased and malignant haematopoietic stem cells
10.1038/s41565-024-01680-8 · 2024 · External reference
In vivo hematopoietic stem cell modification by mRNA delivery
10.1126/science.ade6967 · 2023 · External reference
