Research graph
References from A Cure Out of Most Patients’ Reach — Sickle Cell Disease in the Gene-Therapy Era. Local targets link to admitted publications; unresolved targets remain external evidence.
10.1016/s2352-3026(23)00118-7
10.1016/s2352-3026(23)00118-7 · External reference
10.1056/nejmsa1311707
10.1056/nejmsa1311707 · External reference
10.1182/blood-2016-10-745711
10.1182/blood-2016-10-745711 · External reference
10.1126/science.ade6967
10.1126/science.ade6967 · External reference
10.1182/blood.2025032290
10.1182/blood.2025032290 · External reference
10.1016/s2352-3026(23)00118-7
10.1016/s2352-3026(23)00118-7 · ExternalCitation · doi-reference
10.1056/nejmsa1311707
10.1056/nejmsa1311707 · ExternalCitation · doi-reference
10.1126/science.ade6967
10.1126/science.ade6967 · ExternalCitation · doi-reference
10.1182/blood-2016-10-745711
10.1182/blood-2016-10-745711 · ExternalCitation · doi-reference
10.1182/blood.2025032290
10.1182/blood.2025032290 · ExternalCitation · doi-reference