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References from Cost-effectiveness of etranacogene dezaparvovec compared to eftrenonacog alfa for the treatment of adult patients with severe and moderately severe haemophilia B in Sweden. Local targets link to admitted publications; unresolved targets remain external evidence.
10.1111/bcp.14838
10.1111/bcp.14838 · External reference
10.1111/hae.14046
10.1111/hae.14046 · External reference
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2024 · External reference
10.1111/hae.13998
10.1111/hae.13998 · External reference
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10.1111/hae.14704
10.1111/hae.14704 · External reference
10.1111/jth.15424
10.1111/jth.15424 · External reference
10.1080/13696998.2021.1891088
10.1080/13696998.2021.1891088 · External reference
10.1186/s13023-021-01774-9
10.1186/s13023-021-01774-9 · External reference
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10.1111/hae.70023
10.1111/hae.70023 · External reference
10.1016/j.rpth.2023.100061
10.1016/j.rpth.2023.100061 · External reference
10.1056/nejmoa2211644
10.1056/nejmoa2211644 · External reference
10.1016/s2352-3026(24)00006-1
10.1016/s2352-3026(24)00006-1 · External reference
10.1056/nejmoa2514332
10.1056/nejmoa2514332 · External reference
10.1080/13696998.2020.1721508
10.1080/13696998.2020.1721508 · External reference
10.1007/978-3-540-35280-8_1934
10.1007/978-3-540-35280-8_1934 · External reference
10.1111/hae.13185
10.1111/hae.13185 · External reference
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10.1111/hae.13120
10.1111/hae.13120 · External reference
10.1258/rsmacta.43.5.528
10.1258/rsmacta.43.5.528 · External reference
10.1056/nejmoa1305074
10.1056/nejmoa1305074 · External reference
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A Bayesian approach for selecting relevant external data (BASE): application to a study of long-term outcomes in a hemophilia gene therapy trial (HOPE-B)
2026 · External reference
10.1080/03007995.2022.2133492
10.1080/03007995.2022.2133492 · External reference
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10.1016/j.jval.2012.05.005
10.1016/j.jval.2012.05.005 · External reference
10.1016/j.jval.2016.09.1420
10.1016/j.jval.2016.09.1420 · External reference
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10.2147/ppa.s316276
10.2147/ppa.s316276 · External reference
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10.1016/j.jval.2021.11.1351
10.1016/j.jval.2021.11.1351 · External reference
10.1056/nejmoa2414783
10.1056/nejmoa2414783 · External reference
10.1186/s13023-021-02152-1
10.1186/s13023-021-02152-1 · External reference
10.1111/hae.13003
10.1111/hae.13003 · External reference
10.1007/s40258-024-00932-x
10.1007/s40258-024-00932-x · External reference
10.1080/13696998.2024.2351762
10.1080/13696998.2024.2351762 · External reference
10.1007/s41669-024-00480-z
10.1007/s41669-024-00480-z · External reference
10.18553/jmcp.2024.23214
10.18553/jmcp.2024.23214 · External reference
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10.1186/s13561-018-0185-7
10.1186/s13561-018-0185-7 · External reference
10.1177/0272989x11401031
10.1177/0272989x11401031 · External reference
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10.1007/s40273-017-0580-7
10.1007/s40273-017-0580-7 · External reference
10.1007/s11136-019-02163-3
10.1007/s11136-019-02163-3 · External reference