Research graph

References

References from RNA-targeting therapeutics for rare neuromuscular diseases: progress, challenges, and the path toward personalized treatment. Local targets link to admitted publications; unresolved targets remain external evidence.

10.1371/journal.pone.0261983

10.1371/journal.pone.0261983 · External reference

10.1001/jamaneurol.2016.3388

10.1001/jamaneurol.2016.3388 · External reference

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10.1038/s41419-022-05075-2 · External reference

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10.3389/fbioe.2021.628137/full · External reference

10.1590/1678-4685-gmb-2016-0019

10.1590/1678-4685-gmb-2016-0019 · External reference

10.3233/jnd-210682

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10.3389/fnins.2024.1414658/full · External reference

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10.1016/j.premed.2025.100016 · External reference

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10.1080/15476286.2022.2066334 · External reference

10.3390/genes15070821

10.3390/genes15070821 · External reference

10.1056/nejmoa1813279

10.1056/nejmoa1813279 · External reference

10.1212/wnl.0000000000012998

10.1212/wnl.0000000000012998 · External reference

10.1093/nar/gkag504

10.1093/nar/gkag504 · External reference

10.3390/ph13100294

10.3390/ph13100294 · External reference

10.1038/s41586-023-06277-0

10.1038/s41586-023-06277-0 · External reference

10.3390/pharmaceutics18040446

10.3390/pharmaceutics18040446 · External reference