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10.3390/jcm15051933 · 2026 · External reference

Mucus and inflammation in the HEMT era: persistent barriers to complete airway normalization in cystic fibrosis

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Stop the asthma treatment elevator, we need to get off!

10.1164/rccm.202412-2431vp · 2025 · External reference

Heterogeneity in response to elexacaftor/tezacaftor/ivacaftor in people with cystic fibrosis

10.1016/j.jcf.2024.04.013 · 2024 · External reference

Can AI say “I don’t know”?

10.1056/nejmp2517624 · 2026 · External reference

Change in sweat chloride as a clinical end point in cystic fibrosis clinical trials: the ivacaftor experience

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Elexacaftor/tezacaftor/ivacaftor for cystic fibrosis and rare CFTR variants: in vitro translation to a phase 3, double-blind, randomized, placebo-controlled trial, and real-world study

10.1093/ajrccm/aamaf001 · 2026 · External reference

CFTR modulators and rare variants-leaping from laboratory cells to real world effectiveness?

10.1093/ajrccm/aamaf102 · 2026 · External reference

The French compassionate programme of elexacaftor/tezacaftor/ivacaftor in people with cystic fibrosis with advanced lung disease and no F508del CFTR variant

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Efficacy and safety of CFTR modulators in patients with interstitial lung disease caused by ABCA3 transporter deficiency

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ABC transporters: human disease and pharmacotherapeutic potential

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