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References from Protocol Adherence in Spinal Muscular Atrophy Treated with Nusinersen and Risdiplam: A Retrospective Registry-Based Pharmacoclinical Audit. Local targets link to admitted publications; unresolved targets remain external evidence.
10.1056/nejmoa2009965
10.1056/nejmoa2009965 · External reference
10.1186/s13023-024-03041-z
10.1186/s13023-024-03041-z · External reference
10.1056/nejmoa1702752
10.1056/nejmoa1702752 · External reference
10.1016/s1474-4422(20)30037-5
10.1016/s1474-4422(20)30037-5 · External reference
10.1016/0092-8674(95)90460-3
10.1016/0092-8674(95)90460-3 · External reference
10.1056/nejmoa1710504
10.1056/nejmoa1710504 · External reference
10.1016/s1474-4422(21)00367-7
10.1016/s1474-4422(21)00367-7 · External reference
10.1016/j.nmd.2017.11.004
10.1016/j.nmd.2017.11.004 · External reference
Unresolved reference
External reference
10.1007/s00415-023-11560-1
10.1007/s00415-023-11560-1 · External reference
10.1007/s12325-024-02850-9
10.1007/s12325-024-02850-9 · External reference
10.1212/wnl.0000000000209743
10.1212/wnl.0000000000209743 · External reference
10.1016/j.tins.2020.11.009
10.1016/j.tins.2020.11.009 · External reference